subject area of
- A gene expression phenotype in lymphocytes from Friedreich ataxia patients Academic Article
- Chemical probes identify a role for histone deacetylase 3 in Friedreich's ataxia gene silencing Academic Article
- DNA sequence-specific polyamides alleviate transcription inhibition associated with long GAA.TTC repeats in Friedreich's ataxia Academic Article
- Epigenetic therapy for Friedreich ataxia Academic Article
- Evaluation of histone deacetylase inhibitors as therapeutics for neurodegenerative diseases Academic Article
- Friedreich's ataxia induced pluripotent stem cells model intergenerational GAA.TTC triplet repeat instability Academic Article
- HDAC inhibitors correct frataxin deficiency in a Friedreich ataxia mouse model Academic Article
- Histone deacetylase inhibitors reverse gene silencing in friedreich's ataxia Academic Article
- Long intronic GAATTC repeats induce epigenetic changes and reporter gene silencing in a molecular model of Friedreich ataxia Academic Article
- Pimelic diphenylamide 106 is a slow, tight-binding inhibitor of class i histone deacetylases Academic Article
- Prolonged treatment with pimelic o-aminobenzamide HDAC inhibitors ameliorates the disease phenotype of a Friedreich ataxia mouse model Academic Article
- Quantitative proteomic analysis identifies targets and pathways of a 2-aminobenzamide HDAC inhibitor in Friedreich's ataxia patient iPSC-derived neural stem cells Academic Article
- Rationale for the development of 2-aminobenzamide histone deacetylase inhibitors as therapeutics for Friedreich ataxia Academic Article
- Role of mismatch repair enzymes in GAA.TTC triplet-repeat expansion in Friedreich ataxia induced pluripotent stem cells Academic Article
- Small molecules affecting transcription in Friedreich ataxia Academic Article
- Two new pimelic diphenylamide HDAC inhibitors induce sustained frataxin upregulation in cells from Friedreich's ataxia patients and in a mouse model Academic Article